Replacing the suppressed hormone: toward a better treatment for iron overload in β-thalassemia major? | Haematologica
β-Thalassemia | Genetics in Medicine
A paradigm shift on beta-thalassaemia treatment: How will we manage this old disease with new therapies? - ScienceDirect
Quality of life in patients with β‐thalassemia: A prospective study of transfusion‐dependent and non‐transfusion‐dependent patients in Greece, Italy, Lebanon, and Thailand - Cappellini - 2019 - American Journal of Hematology - Wiley
Significance of genetic modifiers of hemoglobinopathies leading towards precision medicine | Scientific Reports
Cureus | Improving Ineffective Erythropoiesis in Thalassemia: A Hope on the Horizon
Tricuspid-valve regurgitant jet velocity as a risk factor for death in β- thalassemia | Haematologica
Β-Thalassemias | NEJM
Sirolimus for Treatment of β-Thalassemia: From Pre-Clinical Studies to the Design of Clinical Trials
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Cureus | Thalassemia: A Review of the Challenges to the Families and Caregivers
New treatment strategies for β-thalassemia | Encyclopedia MDPI
Current and future alternative therapies for beta-thalassemia major - ScienceDirect
Frontiers | The Future of Gene Therapy for Transfusion-Dependent Beta- Thalassemia: The Power of the Lentiviral Vector for Genetically Modified Hematopoietic Stem Cells
Gene Therapy For Beta-Thalassemia: Updated Perspectives | TACG
Safety and efficacy of thalidomide in patients with transfusion-dependent β- thalassemia: a randomized clinical trial | Signal Transduction and Targeted Therapy
Beta Thalassemia: Practice Essentials, Etiology, Epidemiology
Guidelines for the Management of Transfusion-Dependent Thalassaemia (4th Edition - Version 2.0) by Thalassaemia International Federation (TIF) - Issuu
PDF) Selecting β-thalassemia Patients for Gene Therapy: A Decision-making Algorithm
IJMS | Free Full-Text | Non-Transfusion-Dependent Thalassemia: An Update on Complications and Management
Pathophysiology and treatment of patients with... | F1000Research
Diseases | Free Full-Text | Luspatercept: A New Tool for the Treatment of Anemia Related to β-Thalassemia, Myelodysplastic Syndromes and Primary Myelofibrosis
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
Full article: Revisiting beta thalassemia intermedia: past, present, and future prospects
Cure for thalassemia major – from allogeneic hematopoietic stem cell transplantation to gene therapy | Haematologica
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Current status of beta‐thalassemia and its treatment strategies - Ali - 2021 - Molecular Genetics & Genomic Medicine - Wiley Online Library
